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COMPANY

Ray Therapeutics

HQ: San Francisco, CA source · raytherapeutics.com ↗

Clinical Phase 2

Location: San Francisco, CA · source · May 26, 2023

Profile checked Oct 10, 2026

Keywords: Stargardt Disease Retinitis Pigmentosa Stargardt Macular Dystrophy Geographic Atrophy From Age-related Macular Degeneration Retinal Dystrophies Choroideremia X-linked Retinoschisis X-lined Retinoschisis RTx-021 RTx-015

4Trials (company is sponsor)

Timeline

  1. Trial start —: Development and Evaluation of Functional Visual Field and Navigation Endpoints in Moderate to Profound Inherited Retinal Disease (DEFINE-IRD) source ↗
  2. Trial start 1: Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety of a Single Intravitreal Injection of RTx-021 in Patients With Stargardt Disease source ↗
  3. Trial start Phase 1: Study to Evaluate Safety of RTx-015 Injection in Retinitis Pigmentosa or Choroideremia Patients (ENVISION) source ↗
  4. Trial start —: Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Patients with Retinal Degeneration source ↗

Upcoming milestones

Estimated primary completion per ClinicalTrials.gov. Dates move.

Clinical trials (lead sponsor) 4

RecordTitlePhaseStatusStartPrimary completion
NCT07439887Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety of a Single Intravitreal Injection of RTx-021 in Patients With Stargardt Disease1RecruitingJan 28, 2026Dec 1, 2030 (estimated)
NCT07502664Development and Evaluation of Functional Visual Field and Navigation Endpoints in Moderate to Profound Inherited Retinal Disease (DEFINE-IRD)Not listedRecruitingFeb 19, 20262027-02 (estimated)
NCT06460844Study to Evaluate Safety of RTx-015 Injection in Retinitis Pigmentosa or Choroideremia Patients (ENVISION)Phase 1Active, not recruitingAug 27, 20242030-10 (estimated)
NCT06375239Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Patients with Retinal DegenerationNot listedRecruitingApr 5, 2024Apr 30, 2026 (estimated)
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