COMPANY
NGGT
Timeline
- Trial start Phase 1/Phase 2: AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom) source ↗
Upcoming milestones
- Dec 30, 2030 (ESTIMATED) · Phase 1/Phase 2 · AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom) · NCT06332807
Clinical trials (lead sponsor) 1
| Record | Title | Phase | Status | Start | Primary completion |
|---|---|---|---|---|---|
| NCT06332807 | AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom) | Phase 1/Phase 2 | Recruiting | Jan 10, 2025 | Dec 30, 2030 (estimated) |